We as a family are proud Ambassadors for Cure Rare Disease (CRD). CRD is currently in the beginning stages of creating a custom gene therapy using CRISPR specifically designed for Kal. We are hopeful that the custom gene therapy will allow Kal's body to produce dystrophin, the protein that Kal currently lacks. Without dystrophin, Kal's muscles will continue to degenerate.
Your generous gift will help us fund medical care and equipment not covered by insurance for Kalel.